Media Coverage
Need for better, more specific delivery methods for gene therapies in muscular dystrophy: Melissa Spencer, Ph.D.
Icon
Neurology Live
AAV vectors in gene therapy: Overcoming barriers for muscular dystrophy treatment
Icon
Neurology Live
Health Matters: Bubble boy given new lease on life
Icon
Global News
Atwater girl undergoing innovative treatment
Icon
ABC News
‘Bubble boy’ treatments showing success in spite of funding challenges
Icon
Capitol Weekly
Left in limbo: When pharma halts rare disease research
Icon
Pharmaceutical Technology
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate
Icon
AP News
Kids with 'bubble boy' disease are dying — even though drug companies have found a cure
Icon
Business Insider