Newsroom

Graphic representation of CRISPR-Cas9 repairing the mutation in the gene that causes sickle cell disease (shown in light blue).
Photograph of Evangelina Vaccaro running at the beach
Six of the children who received treatment at UCLA through the gene therapy clinical trials.
Headshot of Donald Kohn
A mix of healthy red blood cells and misshapen cells caused by sickle cell disease. These sickle-shaped cells can clog arteries, producing a range of serious health effects.
Three young siblings don UCLA gear.
Headshot of Donald Kohn in the lab
Sickle Cell clinical trial patient Evie Junior
Headshot of S. Thomas Carmichael on left, headshot of Donald Kohn on right